The genetics-first
drug company.

We develop drugs for targets with proven genetic causality. No more failed trials. Only validated mechanisms.

5/5
Backtest accuracy
10x
vs industry baseline
90%+
Clinical trial failure rate

Drug Development is Broken

90%
Clinical trial failure rate
$2.6B
Average cost per approved drug
12 yrs
Average development time

The industry doesn't have a drug design problem. It has a target selection problem. Companies keep picking targets without genetic validation, then act surprised when trials fail.

Our Approach

We only pursue targets where human genetics proves the mechanism.

Genetic Validation First

Every target in our pipeline has causal genetic evidence. No speculation. No "promising preclinical data." Proof.

Quantified Probability

We know our success probability for each program. Not "high confidence" - actual numbers with uncertainty bounds.

Portfolio Optimization

We allocate capital to programs with the highest expected value. Ruthless prioritization based on genetic evidence strength.

We Prove It Publicly

We make predictions on other companies' trials before outcomes are known. Preregistered. Timestamped. Verifiable.

Drug
Target
Our Call
Readout
DNL788
LRRK2
Success (76%)
H2 2025
AL002
TREM2
Success (72%)
H1 2025
Simufilam
FLNA
Failure (18%)
Q2 2025
Buntanetap
Multiple
Failure (28%)
H1 2025

Backtest on 2023-2024 trials: 5/5 correct. If we can predict their outcomes, imagine what we can do with our own programs.

"Genetically-supported targets have 2x higher clinical success rates"
Nelson et al., Nature Genetics 2015 — validated by King 2019, Minikel 2024

This is the most robust finding in drug development. We're the company built to exploit it.

Any Disease With Genetic Evidence

Mendelian

Single-gene disorders with clear causal variants. Highest confidence targets.

Complex

Polygenic diseases where GWAS + MR identifies causal genes from risk loci.

Multi-Omic

Targets validated across eQTL, pQTL, mQTL, and sQTL for converging evidence.

Disease-modifying therapies only. We don't do symptomatic treatments.

The next generation of drug development.

Built on genetic proof, not hope.